Journal Article Ahead of print
PubMed: 41844555 DOI: 10.1111/bjh.70437
Real-world evidence supports the safety and efficacy profile of luspatercept in clinically complex and heavily iron-overloaded patients.
Br J Haematol
Authors: Barbara Gianesin, Antonietta Zappu, Giovanni Battista Ferrero, Carmen Maria Gaglioti, Michele Santodirocco, Giuseppe Fania, Giovanna Graziadei, Daniele Lello Panzieri, Antonella Massa, Tommaso Mina, Francesca Polese, Angelantonio Vitucci, Francesco Arcioni, Maria Caterina Putti, Valerio Cecinati, Ilaria Fotzi, Paola Maria Grazia Sanna, Antonio Cappello, Filomena Longo, Roberto Lisi, Annamaria Pasanisi, Daniela Pietrasanta, Monica Bocchia, Elisa Bertoni, Antonella Cossu, Marilena Serra, Susanna Barella, Antonia Gigante, Gian Luca Forni, Raffaella Origa
Affiliations
- FORANEMIA ETS Foundation, Genoa, Italy.
- S.C. Centro delle Microcitemie e Anemie Rare, ARNAS G. Brotzu, Cagliari, Italy.
- Thalassemia and Rare Hematological Diseases Centre, San Luigi Gonzaga University Hospital, Orbassano (Torino), Italy.
- Day Hospital Thalassemia, IRCCS "Casa Sollievo della Sofferenza", San Giovanni Rotondo (FG), Italy.
- Immunoematologia e Medicina Trasfusionale (SIMT), IRCCS "Casa Sollievo della Sofferenza", San Giovanni Rotondo (FG), Italy.
- Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, SC Medicina ad Indirizzo Metabolico, Milan, Italy.
- Università degli Studi di Milano, Milan, Italy.
- Servizio Trasfusionale, Ospedale "Giovanni Paolo II", Olbia, Italy.
- Pediatric Hematology/Oncology, Fondazione IRCCS Policlinico San Matteo, Pavia, Italy.
- U.O. Medicina Trasfusionale, Ospedale dell'Angelo, Azienda ULSS 3 Serenissima, Mestre, Venice, Italy.
- Hematology and Bone Marrow Transplantation Unit, AOUC Policlinico, Bari, Italy.
- Pediatric Oncology-Hematology Unit, Santa Maria della Misericordia Hospital, Perugia, Italy.
- Clinic of Pediatric Hematology Oncology, Department of Women's and Children's Health, University Hospital of Padua, Padua, Italy.
- U.O.C. di Pediatria Oncoematologia Pediatrica e Microcitemia, Ospedale Santissima Annunziata, Taranto, Italy.
- U.O.C. "Oncologia, Ematologia e Trapianto di Cellule Staminali Emopoietiche", Meyer Children's Hospital IRCCS, Florence, Italy.
- Servizio Trasfusionale Aziendale, Azienda Ospedaliero-Universitaria di Sassari, Sassari, Italy.
- ASL Novara-Ospedale Ss. Trinità , Borgomanero, Novara, Italy.
- U.O.C. Talassemie ed Emoglobinopatie, Azienda Ospedaliero Universitaria S. Anna, Ferrara, Italy.
- Thalassemia Unit, ARNAS Garibaldi, Catania, Italy.
- U.O.S. Centro Microcitemia "A. Quarta"-U.O.C. Ematologia PO Perrino, Brindisi, Italy.
- Division of Hematology, Azienda Ospedaliera SS Antonio e Biagio e Cesare Arrigo, Alessandria, Italy.
- Department of Medical Science, Surgery and Neuroscience, Hematology, University of Siena, Siena, Italy.
- U.O. Oncoematologia Pediatrica e Trapianto di Midollo Osseo, ASST Spedali Civili di Brescia, Brescia, Italy.
- Centro Microcitemie, Presidio Ospedaliero San Francesco, Nuoro, Italy.
- Internal Medicine Unit, Thalassemia Centre, "Fazzi" Hospital, Lecce, Italy.
- Haematology Unit IRCCS Giannina Gaslini, Genoa, Italy.
- Department of Medical Sciences and Public Health, University of Cagliari, Cagliari, Italy.
MeSH
Thromboembolism, Hematology, Safety