Publications

Journal Article Ppublish

PubMed: 39530361 DOI: 10.1002/ajh.27525

Globalization in clinical drug development for sickle cell disease.

Am J Hematol 100(1):4-9

Authors: Enrico Costa, Russell E Ware, Léon Tshilolo, Julie Makani, Hubert G M Leufkens, Lucio Luzzatto

Affiliations

  • World Health Organization Collaborating Centre for Pharmaceutical Policy and Regulation, Division of Pharmacoepidemiology and Clinical Pharmacology, Utrecht University, Utrecht, The Netherlands.
  • Division of Hematology and Global Health Center, Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, USA.
  • Institut de Recherche Biomédicale 1-Health, CEFA-Monkole, Kinshasa, Congo.
  • Department of Hematology and Blood Transfusion at Muhimbili University of Health and Allied Sciences, Dar es Salaam, Tanzania. Sickleinafrica, Dar-es-Salaam, Tanzania and Imperial College London, London, UK.
  • Regulatory Science and Pharmaceutical Policy, Utrecht University, Utrecht, The Netherlands.
  • Department of Hematology, University of Florence, Florence, Italy.

MeSH

Cells, Drug Development, Hematology, Anemia, Sickle Cell, Pharmaceutical Preparations

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